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Goldberg-Shprintzen syndrome

ICD-10 Codes

Related ICD-10:

R77.1 Q71.03 Q72.00 Q74.0 E76.8 Q37.0 Q92.1 Q32.0 Q72.63 Q31.0 Q72.32 E72.11 H05.403 G71.29 Q70.13 Q16.0 Q04.9 H35.7 M26.09 E23.3 P09.1 H05.413 Q96.0 D81.0 G50.8 H50.18 H17.13 E32.9 Q71.813 Q14.0 N31.2 Q01.8 Q72.11 Q11 Q71.23 H02.211 E07.1 M89.59 H02.514 M26.19 Q79.63 H05.343 Q68.0 H02.519 M61.25 G12.8 J38.01 H50.0 Z87.718 Q38.7 R19.05 G71.0341 Q75.02 E77 E77.9 H55.89 M61.26 M89.29 H02.522 D72.8 M89.21 E88.A E32.8 H02.144 D82 H02.413 H05.3 Q73 H02.824 Q12.4 Q86 E77.8 H05.82 H93.213 H47.20 Q39.3 H02.152 H15.823 Q45.2 H02.14 Z15 Z87.738 H26.03 H05.419 E75.1 E75.11 Q66.80 E31.1 G52.7 M61.24 E76.210 E88.1 S23.170 M94.8X E76.21 H90.A1 M26.5 Q89.4 Q93.2 Q86.0 H02.511 M43.21 E75.29 J34.8211 Q25.3 M61.4 M61.2 Q92.0 Q71.11 Q75.051 H02.40 H15.843 H90.A3 Q85.82 Q73.1 Q75.2 H90 Q24.8 Q66.82 S43.312 Q37.8 Q64.12 Z36.0 E76.22 Q71.0 Q71.01 Q77.6 G71.02 M62.59 G95.0 M85 Q15 Q75.4 Q45.3 Q70.03 M21.73 Q22.8 E72.5 E72.59 H35.723 Q71.12 Q17.8 Q45.0 Q64.72 M94.35 Q97.0 Z31.430 R15.9 Q72.02 F78.A1 Q90.1 E74.05 H83.2X3 Q01.0 Q50.3 H02.422 H02.21C Q91.2 H35.40 Q93.9 H17.03 Q37.1 P09.3 E76.219 Q73.0 Q91.4 H18.463 M89.742 G51.33 H26.04 M20.0 F78 H02.421 Q89.01 E84.11 M40.294 Q25.45 H35.70 H33.23 Q21.22 H02.822 L98.5 E71.42 M61.221 Q00.1 E71.548 M53.2X4 G90.B H49 R13.14 Q39.5 Q32 H05.823 Q71.20 Q21 Q16 Q92.2 M89.37 E34.32 Q82.4 Q77.7 M26.00 H02.439 E71.540 H34.823 J98.6 E74.31 G71.13 Q50.39 E70.8 O28.5 E72.8 O35.05 Q16.3 E72.50 Q17.5 D81.5 Q70.12 Q87.3 K00.0 M40.35 Q52.8 H52.513 H17.823 G71.9 Q70.02 H02.23C M41.53 Q71.812 M89.34 G90.1 Q93.4 Q75.1 Q04.0 M89.741 Q23.3 M61.271 G51.8 Q32.1 Q77.9 Q55.29 M41.54 Q71.6 Q71.89 Q18.9 Q71.3 H02.825 M89.74 S53.12 G71.035 Q71.1 E71.51 E71.518 R62 H51 N27.1 G11 E76 M43.27 Q37 D82.9 Q41.8 Q91.7 E74.820 Q17.1 E16 M62.47 O35.12 D61.8 E74.810 H50.16 Z87.720 Q71.63 Q51.11 R13.12 M61.222 Q35.5 Q78 R63.3 Z13.79 Q98.5 H02.23B Q14.3 Q72.12 K14.4 M41.4 Q87.82 Q18.3 G51.2 H90.A21 Q06.8 Z87.731 N02.6 Q98.9 H05.323 P01.3 Z90.0 H73.81 Q43 Q93.0 M96.89 H35.023 G52 G54.3 M41.55 O30.021 H26.0 H26.09 Q10.3 Q67.4 S23.140 H02.42 Q22 M89.75 H18.033 M89.233 H05.40 H02.22C H02.515 H02.43 H02.432 Q37.4 Q75.002 Q71.2 Q71.21 Q91.0 Q96.2 S11.025 S11.015 Q96.1 M26.72 Q77.4 Q87.8 H05.412 M26.73 E72 H50.17 Q96.8 M53.2X1 Q71.02 H69.83 H47.039 H05.821 Q30.1 Q66.81 H50.689 H35.173 Q87.85 E71.54 Q71.33 Q11.1 Q13.3 Q39 G40.42 M61.272 Q38 Q03.0 N02.1 Q77.8 M62 H05.822 R62.5 Q70.01 Q97.8 H80.13 H02.512 E71.440 Z87.7 H02.155 Q71.32 S23.122 M26.07 M43.25 H35.022 H02.525 M12.41 R47.1 Q71.811 Q93.3 Q90.0 H05.401 Q23 Q72.2 Q25.41 R77.2 H47.22 Q67.1 Q77.2 Q70.23 Q70.11 Q71.00 H02.4 H53.433 H05.402 H54.0X55 N02.3 Q21.23 H44.523 Q36.0 E72.0 Q71.13 K08.23 Q81.1 Q16.9 R68.8 M61.49 Q27 E75.242 H49.0 Q79.1 Q87.19 D35.3 E71.542 E32 G82.5 E71.312 H02.526 R13.0 Q35.3 Q37.2 G70.2 H05.4 Q89.1 H49.3 M26.51 Q15.8 D81.32 H21.243 Q91.1 M89.23 H02.221 Q93.81 Q12.8 Q72.0 E72.89 Q38.3 G25.69 Q71.899 H02.154 G82.53

Description

Goldberg-Shprintzen Syndrome: A Rare Connective Tissue Disorder

Goldberg-Shprintzen syndrome, also known as Shprintzen-Goldberg syndrome (SGS), is a rare and extremely complex connective tissue disorder. It is characterized by a combination of distinctive craniofacial differences, skeletal abnormalities, and intellectual disabilities.

Key Features:

  • Craniofacial differences: Individuals with SGS often have a long, narrow head shape (dolichocephaly), high prominent forehead, widely spaced eyes (hypertelorism), and other facial anomalies.
  • Skeletal abnormalities: Affected individuals may experience scoliosis, long flat feet, and long fingers, among other skeletal issues.
  • Intellectual disabilities: SGS is often associated with intellectual disabilities, ranging from mild to severe.

Other Associated Features:

  • Hirschsprung disease (a condition affecting the large intestine)
  • Marfanoid habitus (a body type characterized by tall stature, long limbs, and a slender build)

Causes and Diagnosis: SGS is caused by mutations in the SKI gene. The diagnosis of SGS can be challenging due to its rarity and complexity.

References:

  • [1] Shprintzen Goldberg syndrome (SGS) is an extremely rare connective tissue disorder characterized by craniofacial differences as well as skeletal and ... (Source 1)
  • [2] Aug 23, 2022 — Shprintzen-Goldberg syndrome is a rare genetic disorder that can cause abnormal facial features, skeletal abnormalities and intellectual ... (Source 2)
  • [3] May 1, 2016 — Affected individuals have a combination of distinctive facial features and skeletal and neurological abnormalities. (Source 3)

Additional Characteristics

  • Intellectual disabilities
  • Skeletal abnormalities
  • Craniofacial differences
  • Hirschsprung disease
  • Marfanoid habitus

Signs and Symptoms

Goldberg-Shprintzen Syndrome (GSS) Signs and Symptoms

Goldberg-Shprintzen syndrome, also known as Shprintzen-Goldberg syndrome, is a rare genetic disorder characterized by distinctive facial features, skeletal abnormalities, and intellectual disability. The condition often presents with a combination of the following signs and symptoms:

  • Facial Features: Individuals with GSS may have a tall, lanky body with increased joint mobility, scoliosis, long flat feet, and long fingers.
  • Skeletal Abnormalities: Affected individuals may experience skeletal abnormalities, including maxillary hypoplasia, hypodontia (missing teeth), high arched palate, short neck, small hands, brachydactyly (short fingers), and fifth finger hypoplasia.
  • Intellectual Disability: GSS is often associated with mild-to-moderate intellectual disability, delayed motor and cognitive milestones.
  • Brain Anomalies: Individuals with GSS may have brain anomalies, including fluid build-up in the brain (hydrocephalus), dilation of the lateral ventricles, and Chiari malformation.

Additional Features

Some individuals with GSS may also experience additional features, such as:

  • Craniosynostosis
  • Craniofacial and skeletal abnormalities
  • Marfanoid habitus
  • Cardiac anomalies
  • Neurological abnormalities

It's essential to note that the severity and presentation of GSS can vary significantly among affected individuals. A comprehensive medical evaluation by a qualified healthcare professional is necessary for an accurate diagnosis and treatment plan.

References:

[1] Aug 23, 2022 — The condition often causes abnormal facial features, skeletal abnormalities and intellectual disability. Being told that your child has SGS can ... [3] May 1, 2016 — Affected individuals have a combination of distinctive facial features and skeletal and neurological abnormalities. A common feature in people ... [7] Shprintzen-Goldberg syndrome (SGS) is characterized by: delayed motor and cognitive milestones and mild-to-moderate intellectual disability; ... [8] Goldberg-Shprintzen megacolon syndrome (GOSHS) is a very rare genetic condition characterized by a swollen, irritated colon (megacolon); characteristic facial ...

Additional Symptoms

  • Maxillary hypoplasia
  • Scoliosis
  • Brachydactyly (short fingers)
  • Short neck
  • Long fingers
  • Mild-to-moderate intellectual disability
  • Tall, lanky body with increased joint mobility
  • Long flat feet
  • Hypodontia (missing teeth)
  • High arched palate
  • Small hands
  • Fifth finger hypoplasia
  • Delayed motor and cognitive milestones
  • Fluid build-up in the brain (hydrocephalus)
  • Dilation of the lateral ventricles
  • Chiari malformation

Diagnostic Tests

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Additional Diagnostic Tests

  • Blood tests
  • Imaging studies

Treatment

Treatment Options for Goldberg-Shprintzen Syndrome

Goldberg-Shprintzen syndrome, also known as Shprintzen-Goldberg syndrome, is a rare genetic disorder that affects multiple systems in the body. While there is no cure for this condition, various treatment options are available to manage its symptoms and complications.

  • Cardiovascular Complications: Individuals with Goldberg-Shprintzen syndrome may experience cardiovascular issues, such as aortic dilatation. In these cases, treatment with beta-adrenergic blockers or other medications can help reduce the risk of complications [5].
  • Surgical Repair: Surgical intervention may be necessary to address specific symptoms, such as developmental delay (DD) and skeletal issues [3].
  • Multidisciplinary Medical Care: A comprehensive treatment approach that involves a team of healthcare professionals, including cardiologists, ophthalmologists, urologists, and orthopedic specialists, can help manage the various aspects of Goldberg-Shprintzen syndrome [3].

While these treatment options can help alleviate symptoms and improve quality of life, it's essential to note that Goldberg-Shprintzen syndrome is a complex condition, and each individual may require a unique treatment plan.

References:

[1] Context result 5: Apr 9, 2020 — If aortic dilatation is present, treatment with beta-adrenergic blockers or other medications should be considered in order to reduce ... [2] Context result 3: Management and treatment. Multidisciplinary medical care and preventive actions, such as treatment of cardiac, ocular, urogenital and skeletal issues and ... [3] Context result 9: Management or Treatment​​ Although Goldberg-Shprintzen syndrome cannot be cured, some of its symptoms can be managed. Cardiovascular complications present the ...

Recommended Medications

  • beta-adrenergic blockers
  • other medications

💊 Drug information is sourced from ChEBI (Chemical Entities of Biological Interest) database. Always consult with a healthcare professional before starting any medication. Click on any medication name for detailed information.

Differential Diagnosis

Differential Diagnoses for Shprintzen-Goldberg Syndrome

Shprintzen-Goldberg syndrome (SGS) can be challenging to diagnose due to its overlapping features with other genetic disorders. The main differential diagnoses include:

  • Marfan syndrome: SGS is often misdiagnosed as Marfan syndrome or Loeys-Dietz syndrome due to the similar facial, skeletal and cardiovascular features [2]. However, intellectual disability and distinctive craniofacial features are more common in SGS.
  • Loeys-Dietz syndrome (LDS): The phenotype of Shprintzen-Goldberg syndrome is often confused with Loeys-Dietz syndrome due to the similar facial, skeletal and cardiovascular features [3]. However, intellectual disability and distinctive craniofacial features are more common in SGS.
  • Mowat-Wilson (MWS) syndrome: Main differential diagnoses include Mowat-Wilson (MWS) and Baraitser-Winter syndromes. Different facial characteristics (thick, horizontal eyebrows and uplifted nasal tip) can help distinguish SGS from these conditions [6].
  • Baraitser-Winter syndrome: This is another condition that shares some similarities with Shprintzen-Goldberg syndrome.

Key Features to Distinguish SGS

To accurately diagnose Shprintzen-Goldberg syndrome, it's essential to look for the following distinctive features:

  • Presence of multiple neonatal fractures, hypoplasia of the nasal bones, femoral bowing, and overlapping fingers [1]
  • Intellectual disability
  • Distinctive craniofacial features (thick, horizontal eyebrows and uplifted nasal tip)
  • Skeletal abnormalities

References

[1] Presence of multiple neonatal fractures, hypoplasia of the nasal bones, femoral bowing, & overlapping fingers helps distinguish this disorder from SGS. HNRNPK ...

[2] SGS is often misdiagnosed as Marfan syndrome or Loeys-Dietz syndrome due to the similar facial, skeletal and cardiovascular features.

[3] Apr 9, 2020 — Differential Diagnosis. Loeys-Dietz syndrome (LDS) and Marfan syndrome (MFS). The phenotype of Shprintzen-Goldberg syndrome (SGS) is often confused with these conditions.

[6] Main differential diagnoses include Mowat-Wilson (MWS) and Baraitser-Winter syndromes. Different facial characteristics (thick, horizontal eyebrows and uplifted nasal tip) can help distinguish SGS from these conditions.

Additional Information

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A syndrome characterized by intellectual disability, specific facial gestalt and Hirschsprung's disease and that has_material_basis_in homozygous mutation in the KIAA1279 gene on chromosome 10q21.1.
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Goldberg-Shprintzen megacolon syndrome
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