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Usher syndrome

ICD-10 Codes

Related ICD-10:

H83.3X1 H59 H21.4 M99.2 Q93.5 H02.519 H11.143 J38.01 H53.6 H53.63 E77.9 H93.3X1 H55.89 H18.319 H35 E77.8 R25.9 H93.0 H57 H18.13 H35.89 H47.20 H33.22 H40.823 H91.8X1 H65.492 I82.55 H02.511 H54.121 H34.11 H35.52 Q87.84 H93 Q31.8 H80.2 H83.8X1 Q75.8 S01.15 H26.413 Z87.72 H90.A3 Q55 H47.49 Q10.6 H18.523 C72.4 Q95.5 E75.09 H81.8X1 Q16.4 H54.2X11 H83 H81.8X2 H54.52A2 H80.1 Z45.321 H21.223 R29.81 H66.3X3 E71.518 H02.516 H35.2 H44.443 H31.413 H54.0X44 Z31.448 H36.89 H93.90 E74.820 H52.519 H53.43 Z87.720 H54.415 H54.415A H72.822 G60.0 H18.831 Q14 Q14.3 Q16.1 S04.6 H35.341 H42 H90.12 H90.A21 G60 Q06.8 I66 H44.51 H53.142 H44.421 H33.011 T26.9 H31.12 H31.121 E71.111 S01.151 G37.8 H18.332 S04.62 H16.41 Q07.8 Q99.9 H83.8X3 H54.12 H81.02 Z45.3 E70.318 H91.8X H35.729 H18.459 I82.451 H16.323 H35.53 H54.42A5 H15.822 H35.311 H50.22 G57.63 F73 H35.361 H53.429 H02.233 H35.021 H83.9 Q16 H91.3 H35.049 G70.9 H54.1215 H93.12 H47.022 R94.120 G44.091 M89.07 H47.13 H54.1142 H21.221 H68.129 H21.249 H91.8 E75.00 H93.3X2 H90.7 H31.129 H83.2X1 H35.371 H90.6 H54.0X33 H33.013 Z83.5 H35.372 H16.412 H81.313 H33.049 H35.029 H16.443 Q80.4 E70.311 H65.493 H53.69 R94.09 H16.033 Z96.21 H53.16 H81.23 H18.021 Q55.4 H80.01 H47.021 H44.513 Q10.4 Q16.0 H53.31 N46.9 J38.02 H83.12 H95.89 H54.42A H47.293 Z13.71 H93.3X3 H90.A11 H54.0X45 H18.832 H35.359 H93.091 H02.231 H83.2X2 H90.42 H21.211 H02.514 H21.272 H18.312 H35.051 Q99.8 H55.02 H90.11 H02.423 H18.892 H83.8 H90.0 H54.1131 H02.43 H47.092 H91.01 H59.343 E70.339 H54.1213 H18.012 H30.133 H65.196 H53.123 Q14.9 H55.8 H83.13 H21.549 T86.8421 H54.414A H18.011 H33.33 H35.353 Q14.1 G40.42 H83.11 G60.3 H68.10 R62.59 H80.13 H16.411 H02.512 H18.89 H40 H93.293 H21.241 H53.462 H18.462 H21.26 S04.819 H54.2 H91.92 Q87 H83.8X2 H54.122 H04.211 H35.42 Q93.3 H53.482 H54.0X43 H18.059 H54.413 H65.4 S04.61 H73.813 H47.22 G51.1 H04.201 H18.893 H02.212 H04.219 R40.211 H83.2X Q92.9 H18.721 H34.8 H53.7 G82.52 H83.8X9 H71.02 H21.552 H83.8X H81.03 Q98.8 H40.023 H47.0 Q16.9 N46.023 H16.441 H49.3 H67.2 H49.43 H31.122 H33.031 H34.833 R94.12 H21.212 P09.6 H33.20 Z31.430 H18.022 H83.2X3 H18.891 Q93.9

Description

Usher Syndrome Description

Usher syndrome is an inherited disorder that causes vision loss, hearing loss, and sometimes balance issues [1]. It is the most common genetic cause of combined deafness and blindness, affecting more than 400,000 people worldwide [7].

The major symptoms of Usher syndrome are:

  • Hearing loss, which can range from mild to complete
  • Vision loss due to an eye disorder called retinitis pigmentosa (RP)
  • Balance issues may also be affected

Usher syndrome is a genetic condition that worsens over time, with vision and hearing loss progressing gradually [4]. It is characterized by progressive vision and hearing loss, making it essential for individuals with the condition to receive proper treatment and management [9].

Key Points:

  • Inherited disorder causing vision loss, hearing loss, and balance issues
  • Most common genetic cause of combined deafness and blindness
  • Hearing loss can range from mild to complete
  • Vision loss due to retinitis pigmentosa (RP)
  • Balance issues may also be affected

References:

[1] Usher syndrome is an inherited disorder that causes vision loss, hearing loss and, sometimes, balance issues. There's no cure, but treatment can help manage ...

[4] Oct 1, 2024 — The major symptoms of Usher syndrome are hearing loss and vision loss from an eye disorder called retinitis pigmentosa, or RP. Vision loss from ...

[7] Usher syndrome is the most common genetic cause of combined deafness and blindness. More than 400000 people are affected by this genetic disorder worldwide.

[9] Usher syndrome is an inherited condition characterized by progressive vision and hearing loss. Balance may also be affected. Symptoms and disease progression ...

Additional Characteristics

  • Hearing loss, which can range from mild to complete
  • Vision loss due to an eye disorder called retinitis pigmentosa (RP)
  • Balance issues may also be affected

Signs and Symptoms

Common Signs and Symptoms of Usher Syndrome

Usher syndrome is a rare inherited disorder that affects both hearing and vision, with some cases also impacting balance. The symptoms can vary depending on the type of Usher syndrome, but common signs include:

  • Hearing Loss: Hearing impairment or deafness is one of the major symptoms of Usher syndrome [1][2].
  • Vision Impairment: Vision loss leading to blindness is another key symptom, caused by retinitis pigmentosa in some cases [3][6].
  • Balance Issues: Some individuals with Usher syndrome may experience balance problems [1].

Additionally, other symptoms may include:

  • Night Blindness: Difficulty seeing in low light conditions
  • Glare Sensitivity: Increased sensitivity to glare or bright lights
  • Needs Contrast: Needing higher contrast between objects and their surroundings to see them clearly
  • Restricted Visual Field: A reduced field of vision
  • Problems with Acuity: Difficulty with visual acuity, which is the sharpness of vision

It's essential to note that symptoms can vary in severity and progression depending on the individual and the specific type of Usher syndrome [4][8].

References: [1] Mar 16, 2017 - Usher syndrome is the most common condition that affects both hearing and vision; sometimes it also affects balance. [2] May 17, 2021 - Usher syndrome is a condition characterized by partial or total hearing loss and vision loss that worsens over time. [3] Oct 1, 2024 - Usher syndrome is the most common genetic condition that affects both vision and hearing. The major symptoms of Usher syndrome are hearing loss and vision loss. [4] Symptoms depend on the type of Usher syndrome. But they often include problems with hearing or deafness, balance, and eyesight or blindness. There are several ... [5] What are Some Symptoms of Usher Syndrome? · Hearing Loss · Night Blindness · Glare Sensitivity · Needs Contrast · Restricted Visual Field · Problems with Acuity. [6] Symptoms of Usher syndrome · hearing impairment and deafness · vision impairment leading to blindness – in Usher syndrome this is caused by retinitis pigmentosa ( ... [7] Oct 1, 2024 - Usher syndrome is the most common genetic condition that affects both vision and hearing. The major symptoms of Usher syndrome are hearing loss and vision loss. [8] Symptoms depend on the type of Usher syndrome. But they often include problems with hearing or deafness, balance, and eyesight or blindness. There are several ...

Additional Symptoms

  • Hearing Loss
  • Night Blindness
  • Vision Impairment
  • Balance Issues
  • Glare Sensitivity
  • Needs Contrast
  • Restricted Visual Field
  • Problems with Acuity

Diagnostic Tests

Diagnostic Tests for Usher Syndrome

Usher syndrome, a rare inherited disorder, can be diagnosed through various tests that assess hearing, vision, and balance. Here are the diagnostic tests used to confirm a diagnosis of Usher syndrome:

  • Hearing Tests: These tests evaluate the extent of hearing loss in individuals with Usher syndrome.
  • Eye Tests: Specifically designed to check for retinitis pigmentosa, these tests help diagnose the visual aspect of Usher syndrome.
  • Balance Tests: Assessing balance and coordination can also be part of the diagnostic process.

Genetic Testing

While not a direct test, genetic testing is crucial in confirming a diagnosis of Usher syndrome. It involves analyzing genes associated with the condition to determine if an individual has inherited mutations that cause the disorder.

Additional Diagnostic Tools

Other tests may be used to support a diagnosis of Usher syndrome, including:

  • Visual Field Test: Measures peripheral (side) vision.
  • Electroretinogram (ERG): Evaluates the response of the retina to light.
  • Electronystagmography (ENG): Assesses balance and eye movement.

These diagnostic tests help healthcare providers confirm a diagnosis of Usher syndrome, enabling them to develop an effective treatment plan for affected individuals.

Additional Diagnostic Tests

  • Genetic Testing
  • Hearing Tests
  • Eye Tests
  • Balance Tests
  • Visual Field Test
  • Electroretinogram (ERG)
  • Electronystagmography (ENG)

Treatment

Current Status of Drug-Based Therapies for Usher Syndrome

Usher syndrome, a genetic disorder affecting hearing and vision, has no approved therapies to prevent vision loss or restore vision. However, researchers are exploring various drug-based treatments to address this condition.

  • Aminoglycosides: Recent studies have shown promising effects of aminoglycosides in cell cultures, which may someday be used as a treatment for Usher syndrome [1].
  • BF844: A Phase I clinical trial has been launched in Perth, Australia, to evaluate the safety and tolerability of BF844, an emerging oral drug, for the treatment of Usher syndrome [2].
  • Gene Therapy: Recent clinical trials are studying a new type of gene therapy that targets one of the most common mutations causing Usher syndrome (USH2A) [5].

Other Investigational Therapies

Several classes of treatments for Usher syndrome are being investigated, including nonsense-mediated therapies. Initial studies focused on nb30, a synthetic compound, but results were inconclusive [3]. Researchers continue to explore alternative approaches.

  • N-acetylcysteine (NAC): A Phase 3 clinical trial has been launched by Johns Hopkins University to evaluate the efficacy of NAC for treating retinitis pigmentosa (RP), a related condition [8].

Support and Management

While there is no cure for Usher syndrome, medical treatments and support services can help individuals with this condition make the most of their abilities. These may include adjustment and career counseling, assistive devices, orientation and mobility training, or communication services [9].

References:

[1] Aminoglycosides Have Promise as Usher Treatment | Drug-Based Therapy News [2] Oct 11, 2024 — A Phase I clinical trial has been launched in Perth, Australia, to evaluate the safety and tolerability of an emerging oral drug known as BF844 for the treatment of Usher syndrome. [3] by LS French · 2020 · Cited by 28 — Several studies have investigated nonsense-mediated therapies for the treatment of Usher syndrome. Initial studies focussed on nb30, a synthetic compound... [5] Nov 15, 2023 — Recent clinical trials are studying a new type of gene therapy that targets one of the most common mutations that cause Usher syndrome (USH2A). [8] Oct 7, 2024 — Johns Hopkins University (JHU) has launched a Phase 3 clinical trial of N-acetylcysteine (NAC) for the treatment of retinitis pigmentosa (RP).

Recommended Medications

  • Gene Therapy
  • Aminoglycosides
  • BF844

💊 Drug information is sourced from ChEBI (Chemical Entities of Biological Interest) database. Always consult with a healthcare professional before starting any medication. Click on any medication name for detailed information.

Differential Diagnosis

Additional Information

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